Tyrosinemia Type I

Definition

Tyrosinemia type I is a metabolic disease characterized by fumarylacetoacetase enzyme deficiency, accompanied by liver failure and renal tubular dysfunction.

Symptoms

  • Liver failure
  • Renal Fanconi syndrome
  • Neurological crises
  • Hypertrophic cardiomyopathy

Reasons

FAH gene mutation.

Diagnosis

Plasma tyrosine, genetic testing.

Treatment

NTBC, dietary restriction.

Which Polyclinic Should You Apply To?

Metabolism Polyclinic

What to Do in an Emergency?

In case of liver failure, emergency services should be consulted.

This page is for general information purposes only.