CPT II Deficiency

Definition

CPT II deficiency is a metabolic disease characterized by long-chain fatty acid oxidation defect and characterized by rhabdomyolysis and myoglobinuria.

Symptoms

  • Exercise intolerance
  • Rhabdomyolysis
  • Myoglobinuria
  • Kidney failure

Reasons

CPT2 gene mutation.

Diagnosis

Muscle biopsy, genetic testing.

Treatment

Dietary modification, MCT oil.

Which Polyclinic Should You Apply To?

Metabolism Polyclinic

What to Do in an Emergency?

In case of rhabdomyolysis, emergency services should be consulted.

This page is for general information purposes only.